Do fair and just systems require compensation for the disadvantages of the natural lottery? a discussion on society's duties on the provision of gene therapy
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Glybera EPAR summary for public https://www.ema.europa.eu/en/medicines/human/EPAR/glybera)Glybera EPAR summary for publichttps://www.ema.europa.eu/en/medicines/human/EPAR/glybera)Search in Google Scholar
Strimvelis EPAR summary for public https://www.ema.europa.eu/en/medicines/human/EPAR/strimvelis)Strimvelis EPAR summary for publichttps://www.ema.europa.eu/en/medicines/human/EPAR/strimvelis)Search in Google Scholar
Aiuti A, Roncarolo MG, Naldini L. Gene therapy for ADA-SCID, the first marketing approval of an ex vivo gene therapy in Europe: Paving the road for the next generation of advanced therapy medicinal products. EMBO Mol Med. 2017; 9(6): 737-740.10.15252/emmm.20170757328396566AiutiARoncaroloMGNaldiniLGene therapy for ADA-SCID, the first marketing approval of an ex vivo gene therapy in Europe: Paving the road for the next generation of advanced therapy medicinal productsEMBO Mol Med201796737740545204728396566Open DOISearch in Google Scholar
Food and Drug Administration. Approval History, Letters, Reviews, and Related Documents. IMLYGIC. 2015 https://www.fda.gov/BiologicsBloodVaccines/CellularGeneTherapyProducts/ApprovedProducts/ucm 469411.htm).Food and Drug Administration. Approval History, Letters, Reviews, and Related DocumentsIMLYGIC2015https://www.fda.gov/BiologicsBloodVaccines/CellularGeneTherapyProducts/ApprovedProducts/ucm469411.htmSearch in Google Scholar
Food and Drug Administration. Approval History, Letters, Reviews and Related Documents. KYM-RIAH. 2017 https://www.fda.gov/Biologics Blood Vaccines/ CellularGeneTherapyProducts/Approved-Products/ ucm573706.htm).Food and Drug Administration. Approval History, Letters, Reviews and Related DocumentsKYM-RIAH2017https://www.fda.gov/Biologics Blood Vaccines/ CellularGeneTherapyProducts/Approved-Products/ucm573706.htm)Search in Google Scholar
Food and Drug Administration. Approval History, Letters, Reviews and Related Documents. YESCARTA. 2017 https://www.fda.gov/BiologicsBloodVaccines/CellularGeneTherapyProducts/ApprovedProducts/ ucm58122 2. htm).Food and Drug Administration. Approval History, Letters, Reviews and Related DocumentsYESCARTA2017https://www.fda.gov/BiologicsBloodVaccines/CellularGeneTherapyProducts/ApprovedProducts/ucm58122 2. htm)Search in Google Scholar
Food and Drug Administration. December 19, 2017 Approval Letter. LUXTURNA. 2017 https://www.fda.gov/BiologicsBloodVaccines/CellularGeneTherapyProducts/ApprovedProducts/ucm589507.htm)Food and Drug Administration. December 19, 2017 Approval LetterLUXTURNA2017https://www.fda.gov/BiologicsBloodVaccines/CellularGeneTherapyProducts/ApprovedProducts/ucm589507.htm)Search in Google Scholar
Flotte TR. Ethical implications of the cost of molecularly targeted therapies. Hum Gene Ther. 2015; 26(9): 573-574.2635541410.1089/hum.2015.29010.trfFlotteTREthical implications of the cost of molecularly targeted therapiesHum Gene Ther201526957357426355414Search in Google Scholar
Regalado A. The world's most expensive medicine is a bust. MIT Technol Rev. 2016 https://www.technologyreview.com/s/601165/the-worlds-most-expensive-medicine-is-a-bust/RegaladoAThe world's most expensive medicine is a bustMIT Technol Rev2016https://www.technologyreview.com/s/601165/the-worlds-most-expensive-medicine-is-a-bust/Search in Google Scholar
Rawls JA. Theory of Justice (original ed). Cambridge, MA, USA: The Belknap Press, 2005; 60-65; 118-142.RawlsJATheory of Justice (original ed)Cambridge, MA, USAThe Belknap Press200560-65118142Search in Google Scholar
O'Brian WE Jr. Equality in law and philosophy. Inquiry. 2010; 53(3): 257-284. doi: 10.1080/00201741003784648.10.1080/00201741003784648O'BrianWE JrEquality in law and philosophyInquiry201053325728410.1080/00201741003784648Open DOISearch in Google Scholar
Buchanan A, Brock DW, Daniels N, Wilker D. From Chance to Choice. Genetics and Justice. Cambridge, Cambridgeshire, UK: University Press, 2000.BuchananABrockDWDanielsNWilkerDFrom Chance to Choice. Genetics and JusticeCambridge, Cambridgeshire, UKUniversity Press200010.1017/CBO9780511806940Search in Google Scholar
Daniels N. Just Health: Meeting Health Needs Fairly. New York, NY, USA: Cambridge University Press, 2008.DanielsNJust Health: Meeting Health Needs FairlyNew York, NY, USACambridge University Press2008Search in Google Scholar
Arneson RJ. Luck egalitarianism interpreted and defended. Philosophical Topics. 2004; 32(1-2): 1-20.10.5840/philtopics2004321/217ArnesonRJLuck egalitarianism interpreted and defendedPhilosophical Topics2004321-2120Open DOISearch in Google Scholar
Ekmekci PE, Arda, Β. Luck egalitarianism, individual responsibility and health. Balkan Med J. 2015; 32(3): 244-254.2618571110.5152/balkanmedj.2015.150012EkmekciPEArdaΒLuck egalitarianism, individual responsibility and healthBalkan Med J2015323244254449768926185711Search in Google Scholar
