Rare Neurological Diseases: an Overreview of Pathophysiology, Epidemiology, Clinical Features and Pharmacoeconomic Considerations in the Treating

Publié en ligne: 26 déc. 2021

Reçu: 07 juil. 2021

Accepté: 22 août 2021

DOI: https://doi.org/10.2478/sjecr-2021-0049

Mots clés

Rare diseases, Dravet syndrome, Tuberous sclerosis complex, Lennox-Gastaut syndrome, Angelman syndrome, Prader-Willi syndrome, Duchenne Muscular Dystrophy, Spinal muscular atrophy, orphan drugs, pharmacoeconomics

© 2020 Medo Gutic et al., published by Sciendo

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