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The potential impact of gene therapy on health-related quality of life (HRQoL) domains in haemophilia

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30 mai 2021
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Bullinger, Monika ORCID Icon
Gardner, Diandra Latibeaudiere ORCID Icon
ICON Clinical Research LimitedLondon, UK
Lewis, Hannah B ORCID Icon
ICON Clinical Research LimitedLondon, UK
Miesbach, Wolfgang ORCID Icon
Medical Clinic 2, Institute of Transfusion Medicine, University Hospital FrankfurtGermany
Nolte, Sandra ORCID Icon
ICON Clinical Research Limited, Charité–Universitätsmedizin Berlin, corporate member of Freie Universität Berlin, Humboldt-Universität zu Berlin, Berlin Institute of Health, Medical Department, Division of Psychosomatic MedicineMunich
O’Hara, Jamie ORCID Icon
HCD Economics, University of ChesterUK
O’Mahony, Brian ORCID Icon
Irish Haemophilia Society, Trinity CollegeDublin
Pollard, Debra ORCID Icon
Royal Free Hospital, Trustee of Haemnet, MASAG, European Haemophilia ConsortiumLondon
Skinner, Mark ORCID Icon
Institute for Policy Advancement Ltd, McMaster UniversityWashington
Quinn, Jennifer ORCID Icon
BioMarin UK LtdLondon, UK