<abstract xmlns="http://www.w3.org/1999/xhtml"><p> The history of haemophilia care has been fraught with extreme successes and epic failures. The development of plasmaderived concentrates made prophylactic treatment and home care possible, but the unintended consequences were devastating for a generation and only abated with the emergence of recombinant products. Now with the arrival of longer-acting factor concentrates and the potential offered by gene therapy, further improvements in medical and social outcomes are possible. But these new treatment approaches raise challenging ethical and moral issues that society must be prepared to confront.</p></abstract>

The history of haemophilia care has been fraught with extreme successes and epic failures. The development of plasmaderived concentrates made prophylactic treatment and home care possible, but the unintended consequences were devastating for a generation and only abated with the emergence of recombinant products. Now with the arrival of longer-acting factor concentrates and the potential offered by gene therapy, further improvements in medical and social outcomes are possible. But these new treatment approaches raise challenging ethical and moral issues that society must be prepared to confront.

The impending medical revolution in haemophilia care: one patient’s view

The Journal of Haemophilia Practice

This work is licensed under the Creative Commons Attribution-NonCommercial-NoDerivatives 4.0 License.

{"article-title":"The impending medical revolution in haemophilia care: one patient\u2019s view"}

The history of haemophilia care has been fraught with extreme successes and epic failures. The development of plasmaderived concentrates made prophylactic...

The impending medical revolution in haemophilia care: one patient’s view

Article Category: Gene Therapy

Published Online: Apr 21, 2018

Page range: 9 - 11

DOI: https://doi.org/10.17225/jhp.00041

Keywords
haemophilia, haemophilia B, Christmas disease, gene therapy, long-acting clotting factor

© 2018

This work is licensed under the Creative Commons Attribution-NonCommercial-NoDerivatives 4.0 License.

The impending medical revolution in haemophilia care: one patient’s view

Article Category: Gene Therapy

Published Online: Apr 21, 2018

Page range: 9 - 11

DOI: https://doi.org/10.17225/jhp.00041

Keywordshaemophilia, haemophilia B, Christmas disease, gene therapy, long-acting clotting factor

© 2018

This work is licensed under the Creative Commons Attribution-NonCommercial-NoDerivatives 4.0 License.

Keywords
haemophilia, haemophilia B, Christmas disease, gene therapy, long-acting clotting factor